Innovative COA tools to reduce steroid toxicity in autoimmune care
Collaboration to leverage Steritas’ STOX Suite in developing innovative treatments for autoimmune diseases.
Archives for November 19, 2024
Serious adverse event causes problems for Neurogene’s Rett gene therapy
A serious adverse event in the New York biotech’s phase 1/2 trial of its Rett syndrome gene therapy puts a question mark over the program.
FDA approves first-ever gene therapy to be directly administered to the brain
PTC Therapeutics has received FDA approval for a gene therapy to treat AADC deficiency, a rare genetic disorder that impairs the normal function of neurons.