Rare Disease Day
The race for answers: How a Dutch university is reducing time to identify rare diseases
Being able to identify rare diseases is challenging especially since more than 80% of them have genetic origins.
Archives for February 29, 2024
Nezglyal remains 'promising' therapy despite EMA’s market authorization refusal
The European Medicines Agency’s (EMA) Committee for Medicinal Products for Human Use (CHMP) recently refused marketing authorization for Nezglyal (leriglitazone).